Beta
49264

Efficacy and Safety of Eltrombopag for the Treatment of Chronic Idiopathic Thrombocytopenic Purpura in Children and Adolescents

Article

Last updated: 30 Jan 2023

Subjects

-

Tags

-

Abstract

Background: Chronic ITP is a very common disease in children. Most treatment options have focused on slowing platelet destruction like corticosteroids and IVIG. These treatments are not always effective, or have only a transient effect, and treatment related adverse events often restrict further use. Impaired platelet production has been evolved as a potential disease mechanism for ITP. As a result, growth factor and growth factor analogue stimulation of megakaryopoiesis has also been investigated. Objective: is to evaluate the efficacy and safety of eltrombopag for the treatment of children and adolescents with chronic ITP. Subjects and methods: It was a prospective cohort study which was conducted on forty patients (22 males and 18 females) with chronic ITP. They were treated with eltrombopag for a period ranged from 6 months to 2 years after failure of first line of treatment (steroids, IVIG or both). Patients started eltrombopag with mean initial platelet count 14.4 X 103 / uL and were evaluated after at least 6 months of therapy. The study was approved by the academic and medical ethics committee of Zagazig University and a written informed consent was obtained from all patients. Results: Thirty patients (75%) responded to eltrombopag with a mean platelet count of 100.9 X103/ uL while 10 patients (25%) did not respond to the drug. Mean platelet count was significantly higher after eltrombopag therapy (100.9 ± 65.97 versus 14.4 ± 8.87, P < 0.001). The longer the duration of treatment, the higher the mean platelet count after treatment (r = 0.4, P < 0.001). Only 43.3% of responders received combined treatment with IVIG and steroids versus 20% of non-responders (p = 0.006). Conclusion: Eltrombopag is an effective, well tolerated and safe drug to restore platelet counts at levels high enough to prevent bleeding events in children with chronic ITP.

DOI

10.21608/ejhm.2019.49264

Keywords

Eltrombobag, Chronic ITP, Treatment, children, Efficacy, safety

Authors

First Name

Tamer Hasan

Last Name

Hassan

MiddleName

-

Affiliation

Department of Pediatrics, Faculty of Medicine, Zagazig University

Email

-

City

-

Orcid

-

First Name

Marwa Zakaria

Last Name

Mohamed

MiddleName

-

Affiliation

Department of Pediatrics, Faculty of Medicine, Zagazig University

Email

-

City

-

Orcid

-

First Name

Sameh Nabil Khalil

Last Name

Nada

MiddleName

-

Affiliation

Department of Pediatrics, Faculty of Medicine, Zagazig University

Email

merna.emad.roshdy@gmail.com

City

-

Orcid

-

Volume

77

Article Issue

2

Related Issue

7349

Issue Date

2019-10-01

Receive Date

2019-09-23

Publish Date

2019-10-01

Page Start

5,068

Page End

5,073

Print ISSN

1687-2002

Online ISSN

2090-7125

Link

https://ejhm.journals.ekb.eg/article_49264.html

Detail API

https://ejhm.journals.ekb.eg/service?article_code=49264

Order

29

Type

Original Article

Type Code

606

Publication Type

Journal

Publication Title

The Egyptian Journal of Hospital Medicine

Publication Link

https://ejhm.journals.ekb.eg/

MainTitle

-

Details

Type

Article

Created At

22 Jan 2023